The US Food and Drug Administration (FDA) has released draft guidance on how sponsors can utilize next-generation sequencing ...

The ACC has published a scientific statement regarding the use of gene editing therapy for cardiovascular disease.

A domestically developed gene-editing therapy has successfully treated patients with beta-thalassemia, allowing them to live ...

This guidance emphasises the potential of NGS methods in mitigating safety risks associated with therapies incorporating ...

Forbes contributors publish independent expert analyses and insights. A patient in a late-stage gene editing trial for a rare heart condition died from fatal liver complications after receiving an ...

For the millions of people living with genetic diseases like muscular dystrophy and inherited liver disorders, one of the ...

The baby saved from a rare disease by a first-ever personalized gene fix has reached a big milestone, taking his first steps ahead of Christmas. KJ Muldoon is walking and getting ready to celebrate ...

A research team has discovered an enhanced CRISPR gene-editing system that could enable targeted delivery inside the human ...

The FDA’s recently unveiled plausible mechanism framework may have been forged with i | The FDA’s newly launched plausible ...

KJ Muldoon, a 10-month-old baby who sparked nationwide headlines after receiving a first-of-its kind gene-editing treatment, was released from the hospital this week. KJ has spent the majority of his ...

Scientists have taken an important step toward a gene therapy that could one day turn off the extra genetic material that ...