As early results show promise, the 23-year-old hopes the treatment could finally clear a path toward his dream of becoming ...

Sickle Cell disease can be a very scary issue to deal with however, with proper monitoring and care, many people are able to live their life to its full capacity with minor complications. According to ...

After six weeks in the hospital, 23‑year‑old Daniel Cressy leaves with hope for a functional cure and a future where he can ...

Learn about the groundbreaking gene therapy for sickle cell disease at Manning Family Children's Hospital in Louisiana, ...

Dr. Swee Lay Thein and Dr. Stuart Orkin won the $3 million Breakthrough Prize in Life Sciences for their work toward a ...

Heather Avant always dresses up when she goes to the emergency room. Subscribe to read this story ad-free Get unlimited access to ad-free articles and exclusive content. “I’ve been conditioned to act ...

Novo Nordisk is gearing up to submit its rare blood disorder drug to the FDA after the former Forma Therapeutics asset ...

Share on Pinterest There may soon be a new treatment for sickle cell anemia that uses gene-editing techniques that could potentially cure the disease. SDI Productions/Getty Images For the first time, ...

Novo Nordisk’s etavopivat elicited a 27% drop in vaso-occlusive crises and 48.7% hemoglobin response after 24 weeks, creating ...

Patients with sickle cell disease may experience potentially dangerous gaps in care across the NHS as understanding of the condition remains limited, a health care safety watchdog has warned. The ...

Sickle cell anemia may not be as well-known as, say, malaria, tuberculosis or AIDS. But every year, hundreds of thousands of babies around the world are born with this inherited blood disorder. And ...

Q1 2026 Management View Brian Goff (CEO & Director) said the company is “off to a strong start entering another catalyst-rich year,” highlighting $20.7 million in net revenues and “138% growth ...